Gene therapy for sickle cell disease (Review) .https://www.cochranelibrary.com/cdsr/doi/10.1002/14651858.CD007652.pub7/full

The objectives of this review are to:

1.- Determine whether gene therapy can improve survival and prevent symptoms and complications associated with SCD;

2.- Examine the risks of gene therapy against the potential long‐term gain for people with SCD.